Mitochondrial disease study shows positive interim… - The Lily Foundation
The Lily Foundation logo featuring a butterfly, hearts and an 'x' for a kiss

Fighting mito,
finding hope.

Mitochondrial disease study shows positive interim results

Research

19 July 2024

A clinical trial looking to develop an effective treatment for mitochondrial diseases has shown positive interim results and The Lily Foundation are encouraged to hear that it’s been given the go-ahead to continue.

Close-up of a group of empty test tubes against a purple background

Abliva, a Swedish pharmaceutical company who develop medicines for the treatment of mitochondrial diseases, announced this week that interim analysis of their FALCON study has been positive, with independent body the Data Monitoring Committee recommending that the study continue without any modification.

The study is investigating whether the company’s newly developed drug, KL1333, can improve the symptoms of chronic fatigue and myopathy (muscle weakness) in adult patients living with a genetic diagnosis of mitochondrial disease.

The Lily Foundation’s Research Manager Maria commented on the news: “Clinical research studies like this one are crucial in the path to discovering treatments for mitochondrial disease, so we’re encouraged to hear this positive step. We know a number of patients from within our mito community are part of this study at sites in Cambridge, UCL and Newcastle, and having supported the initial recruitment to the trial, we’re pleased to hear of its progress.”

We wish the Abliva team continued success with the study and look forward to future updates.

Read Abliva’s press release.

Donate today

Donate through JustGiving to help us continue funding life-changing research – it’s our best hope of finding effective treatments to improve the lives of mitochondrial disease patients.